Ultragenyx clinical studies in development for Glut1 DS
UX007 (highly purified synthetic 7-carbon fatty acid triglyceride)
UX007 is a highly purified, odorless, tasteless oil that is mixed with food or drink. Clinical studies are ongoing to determine if UX007 is safe and effective in treating Glut1 DS. When the studies are completed, the research will be submitted to the regulatory agencies for possible approval as a treatment for Glut1 DS.
This treatment is investigational and has not yet been approved for use by any regulatory agency. Efficacy and safety have not been established. The information presented should not be construed as a recommendation for use.
Learn about current ongoing clinical studies for Glut1 DS
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